Table 5. Gene frequency in Colombian subgroup.
Gene Disease n %
SERPINA1 Alpha-1 antitrypsin deficiency 80 11.3
CYP21A2 Congenital adrenal hyperplasia due to 21-hydroxylase deficiency 72 10.2
HBA2 Alpha thalassemia 67 9.5
HBA1/HBA 2 Alpha thalassemia 2 0.3
HBA1 Alpha thalassemia 1 0.1
HBA Alpha thalassemia 1 0.1
CFTR Cystic fibrosis 49 6.9
SMN1 Spinal muscular atrophy type 1 43 6.1
ABCA4 Stargardt's disease type 1; cone-rod dystrophy type 3 36 5.1
GJB2 Autosomal recessive non-syndromic sensorineural deafness, type DFNB 15 2.1
ATP7B Wilson's disease 14 2.0
CBS Homocystinuria due to cystathionine beta-synthase deficiency 13 1.8
CFTR Bilateral congenital absence of the vas deferens 13 1.8
G6PD Glucose-6-phosphate dehydrogenase deficiency 13 1.8
ACADM Medium-chain acyl-CoA dehydrogenase deficiency 11 1.6
OCA2 Oculocutaneous albinism type 1A 10 1.4
PMM2 Congenital disorder of glycosylation type 1a 10 1.4
TYR Oculocutaneous albinism type 1A 9 1.3
SBDS Shwachman-Diamond Syndrome 8 1.1
SLC26A2 Atelosteogenesis type 2 8 1.1
GAA Glycogen storage disease due to acid maltase deficiency (Pompe disease) 7 1.0
CLCN1 Autosomal recessive myotonia congenita 6 0.8
COL7A1 Dystrophic epidermolysis bullosa (EAD) Hallopeau-Siemens (HS) and non-HS type; puriginous EAD; pretibial EDA 6 0.8
HEXA Tay/Sachs disease 6 0.8
MEFV Mediterranean fever 6 0.8
TMPRSS3 Autosomal recessive non-syndromic sensorineural deafness, type DFNB10 6 0.8
ADA Severe combined immunodeficiency due to adenosine deaminase (ADA) deficiency 5 0.7
BCHE Butyrylcholinesterase deficiency 5 0.7
BTD Biotinidase deficiency 5 0.7
FIG4 Charcot-Marie-Tooth disease type 4J 5 0.7
GDAP1 Charcot-Marie-Tooth disease type 4A 5 0.7
HBB Sickle cell anemia 5 0.7
ACADS Short-chain acyl-CoA dehydrogenase deficiency 4 0.6
FAH Tyrosinemia type 1 4 0.6
FMR1 Fragile X syndrome 4 0.6
GALC Krabbe disease 4 0.6
GNPTAB Mucolipidosis type 2 alpha/beta; Mucolipidosis type 3 alpha/beta 4 0.6
GNRHR Hypogonadotropic hypogonadism type 7 4 0.6
HBB Beta thalassemia 4 0.6
POLR1C Treacher-Collins syndrome 4 0.6
SPG7 Autosomal recessive spastic paraplegia type 7 4 0.6
ACADSB 2-methylbutyryl-CoA dehydrogenase deficiency 3 0.4
ALDOB Hereditary fructose intolerance 3 0.4
CNGB3 Acromatopsia 3 3 0.4
COL4A3 Autosomal recessive Alport syndrome 3 0.4
DCLRE1C Omenn syndrome; Severe combined immunodeficiency Athabaskan type 3 0.4
GALNS Mucopolysacchariosis type 4A 3 0.4
GJB2 Autosomal recessive hearing loss type 1A; Digenic hearing loss GJB2/GJB6 3 0.4
OTOF Autosomal recessive nonsyndromic sensorineural deafness, type DFNB9 3 0.4
PAH Phenylketonuria 3 0.4
RPGRIP1L Joubert syndrome type 7; Meckel syndrome type 5; COACH Syndrome 3 0.4
SMPD1 Niemann-Pick disease type A; Niemann-Pick disease type B 3 0.4
UGT1A1 Crigler-Najjar syndrome type 2 3 0.4
AGL Glycogen storage disease type 3 2 0.3
AIPL1 Leber congenital amaurosis 4 2 0.3
AR Partial androgen insensitivity syndrome 2 0.3
ARSB Mucopolysaccharidosis type 6 (Maroteaux-Lamy syndrome) 2 0.3
CAPN3 Autosomal recessive limb-girdle muscular dystrophy type 2A 2 0.3
CHST6 Macular corneal dystrophy 1 2 0.3
CNGB1 Retinitis pigmentosa 39 2 0.3
CYP27A1 Cerebrotendinous xanthomatosis 2 0.3
DHCR7 Smith-Lemli-Opitz syndrome 2 0.3
DYSF Miyoshi muscular dystrophy type 1; autosomal recessive limb-girdle muscular dystrophy type 2 (LGMD2) 2 0.3
GALE Galactose epimerase deficiency 2 0.3
GBA Gaucher disease 2 0.3
HGSNAT Mucopolysacchariosis type 3, Sanfilippo Syndrome type C 2 0.3
MYO15A Autosomal recessive deafness type 3 2 0.3
NR2E3 Enhanced Cone-S syndrome (Goldmann-Favre); Retinitis pigmentosa type 37 2 0.3
PKHD1 Polycystic kidney disease type 4 2 0.3
SLC22A5 Systemic primary carnitine deficiency 2 0.3
SPG11 Juvenile amyotrophic lateral sclerosis, type 5 2 0.3
USH2A Retinitis pigmentosa 39 2 0.3
USH2A Usher syndrome type 2A 2 0.3
ACADVL Very long chain acyl-CoA dehydrogenase deficiency 1 0.1
ACSF3 Combined malonic and methylmalonic acidemia 1 0.1
AHI1 Joubert syndrome 3 1 0.1
ALG3 Congenital disorder of glycosylation type Id 1 0.1
ALG12 Congenital disorder of glycosylation type Ig 1 0.1
ARSA Metachromatic leukodystrophy 1 0.1
ATM Ataxia telangiectasia 1 0.1
ASS1 Citrullinemia type 1 1 0.1
CERKL Retinitis pigmentosa 26 1 0.1
CEP290 Meckel syndrome type 4; Joubert syndrome type 5; Leber congenital amaurosis type 10 1 0.1
CPT2 Carnitine palmitoyl palmitoyltransferase deficiency type 2, neonatal lethal form; Carnitine palmitoyltransferase deficiency type 2, infantile form 1 0.1
CYP1B1 Primary congenital glaucoma type 3A 1 0.1
DMD Duchenne muscular dystrophy 1 0.1
DOK7 Fetal akinesia deformation sequence type 3; congenital myasthenic syndrome type 10 1 0.1
DNAH5 Primary ciliary dyskinesia type 3 1 0.1
FH Fumaric aciduria 1 0.1
FANCG Fanconi anemia complementation group G 1 0.1
GALT Galactosemia 1 0.1
GAMT Cerebral creatine deficiency syndrome type 2 1 0.1
GCDH Glutaric acidemia type 1 1 0.1
GBBS10 Bardet Bieldl syndrome type 1 1 0.1
GFM1 Hepatoencephalopathy due to combined oxidative phosphorylation deficiency type 1 1 0.1
GLA Fabry disease 1 0.1
HADHA Deficiency of 3-hydroxyacyl-CoA dehydrogenase of long-chain fatty acids 1 0.1
GRHPR Primary hyperoxaluria type 2 1 0.1
HBB HBB-related hemoglobinopathies 1 0.1
HDD Sickle cell anemia 1 0.1
IVD Isovaleric acidemia 1 0.1
IDUA Hurler syndrome 1 0.1
LOXHD1 Autosomal recessive deafness type 77 1 0.1
HOGA1 Primary hyperoxaluria type 3 1 0.1
MMACHC Methylmalonic acidemia with homocystinuria type cblC 1 0.1
MVK Mevalonic aciduria 1 0.1
MPDU1 Congenital disorder of glycosylation 1F 1 0.1
MTHFR Homocystinuria due to MTHFR deficiency 1 0.1
NLRP7 Recurrent hydatidiform mole type 1 1 0.1
NPC1 Niemann-Pick disease type C1 1 0.1
PCDH15 Usher syndrome type 1F 1 0.1
PEX12 Peroxisome biogenesis disorder type 3A (Zellweger spectrum) 1 0.1
PCCA Propionic acidemia 1 0.1
POLG POLG-realated disorders 1 0.1
PROP1 Panhypopituitarism 1 0.1
POMT1 Congenital muscular dystrophy-dystroglycanopathy type 1A (Walker/ Warburg syndrome); type 1B; Type 1C (autosomal recessive limb-girdle muscular dystrophy type 11 (LGMD R11) 1 0.1
SAG Oguchi disease 1 0.1
SCO2 Fatal infantile cardioencephalomyopathy due to cytochrome c oxidase 1 deficiency. 1 0.1
SGSH Mucopolysaccharidosis type 3A 1 0.1
SH3TC2 Charcot-Marie-Tooth disease type 4C 1 0.1
SLC12A3 Gitelman syndrome 1 0.1
SLC26A4 Autosomal recessive deafness type 4; Pendred Syndrome 1 0.1
SUMF1 Multiple sulfatase deficiency 1 0.1
TRDN Catecholaminergic polymorphic ventricular tachycardia 5 1 0.1
TREX1 Aicardi-Goutieres syndrome type 1 1 0.1
UGT1A1 Crigler-Najjar syndrome type 1 1 0.1