Diseases Female-Donors Male-Donors Reference (Recombine)
Cystic Fibrosis 1:24 1:29 1:48
No syndromic Hearing Loss and Deafness: GJB2 Related 1:30 1:15 1:25
Biotinidase Deficiency 1:35 1:29 1:123
Spinal Muscular Atrophy: SMN1 Linked 1:27 0 1:55
Fumarase Deficiency 0 1:29 1:500
21HydroxylaseDeficient      
Nonclassical Congenital Adrenal Hyperplasia 1:13 0 1:4
Familial Mediterranean Fever 1:51 1:29 1:4/1:80
Pseudocholinesterase Deficiency 1:51 1:15 1:33